Orchard Therapeutics plc (NASDAQ:ORTX) and Pharming Group NV (NASDAQ:PHAR) have collaborated to research, develop, manufacture and commercialize OTL-105 for hereditary angioedema (HAE). OTL-105 is…
Expected clinical package for OTL-200 BLA for MLD using data from existing patients clarified with FDA
Guidance obtained on design of OTL-203 global registrational trial for MPS-IH
Enrollment goal met in OTL-201