Administration of one-time hematopoietic stem cell (HSC) gene therapy resulted in sustained, clinically meaningful benefits by preserving cognitive function and motor development in most patients
90% overall survival
Orchard Therapeutics (NASDAQ:ORTX) reported quarterly losses of $(0.29) per share. This is a 45 percent decrease over losses of $(0.20) per share from the same period last year.
Orchard Therapeutics (NASDAQ:ORTX), a global gene therapy leader, today announced the acceptance of nine abstracts at the upcoming European Society of Gene & Cell Therapy Congress (ESGCT) taking place virtually from